Mild phenotype in an adult male with X‐linked adrenoleukodystrophy – case report

نویسندگان

  • Morten A. Horn
  • Karin B. M. Mikaelsen
  • Sacha Ferdinandusse
  • Ellen Jørum
  • Svein I. Mellgren
  • Lars Retterstøl
  • Ronald J. A. Wanders
  • Chantal M. E. Tallaksen
چکیده

X-linked adrenoleukodystrophy may present with a deceptively mild phenotype, even in adult males. Tight collaboration between clinicians, geneticists, biochemists, and other specialists is increasingly required for clarification of diagnosis in cases with atypical presentation.

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عنوان ژورنال:

دوره 4  شماره 

صفحات  -

تاریخ انتشار 2016